Long-term enzyme replacement therapy with velmanase alfa (human recombinant alpha-mannosidase) slows disease progression in adult patients suffering from alpha-mannosidosis-Reference-Cited by-同舟云学术

Long-term enzyme replacement therapy with velmanase alfa (human recombinant alpha-mannosidase) slows disease progression in adult patients suffering from alpha-mannosidosis

Published:2017-01 Issue:1-2 Volume:120 Page:S30
ISSN:1096-7192
Container-title:Molecular Genetics and Metabolism
language:en
Short-container-title:Molecular Genetics and Metabolism

Author:

Borgwardt Line,Lund Allan M,Amraoui Yasmina,Andersen Oluf,De Meirleir Linda,Dolhem Philippe,Campos Mercedes Gil,Guffon Nathalie,Héron Bénédicte,Laroche Cecile,Lindberg Christoffer,Marquardt Thorsten,Mengel Karl-Eugene,Muschol Nicole,Tylki-Szymanska Anna,Van Den Hout Johanna MP,Der Ploeg Ans Van,Welling Lindsey,Wijburg Frits,Cole Duncan,Fogh Jens,Geraci Silvia,Ardigò Diego,Cattaneo Federica

Publisher

Elsevier BV

Subject

Endocrinology,Genetics,Molecular Biology,Biochemistry,Endocrinology, Diabetes and Metabolism

Cited by 4 articles. 订阅此论文施引文献订阅此论文施引文献，注册后可以免费订阅5篇论文的施引文献，订阅后可以查看论文全部施引文献

1. Response to the Letter to the Editor concerning ‘Cost-effectiveness of velmanase alfa vs. bone marrow transplantation or no causal therapy in patients with mild to moderate alpha-mannosidosis’;Biotechnology & Biotechnological Equipment;2024-08

2. Cost-effectiveness of velmanase alfa vs. bone marrow transplantation or no causal therapy in patients with mild to moderate alpha-mannosidosis;Biotechnology & Biotechnological Equipment;2023-10-23

3. Caregivers’ and Physicians’ Perspectives on Alpha-Mannosidosis: A Report from Italy;Advances in Therapy;2020-11-24

4. Alpha-Mannosidosis: Therapeutic Strategies;International Journal of Molecular Sciences;2018-05-17