Health-related quality of life following valoctocogene roxaparvovec gene therapy for severe hemophilia A in the phase 3 trial GENEr8-1-Reference-Cited by-同舟云学术

Health-related quality of life following valoctocogene roxaparvovec gene therapy for severe hemophilia A in the phase 3 trial GENEr8-1

Published:2023-12 Issue:12 Volume:21 Page:3450-3462
ISSN:1538-7836
Container-title:Journal of Thrombosis and Haemostasis
language:en
Short-container-title:Journal of Thrombosis and Haemostasis

Author:

O’Mahony Brian,Dunn Amy L.,Leavitt Andrew D.,Peyvandi Flora,Ozelo Margareth C.,Mahlangu Johnny,Peerlinck Kathelijne,Wang Jiaan-Der,Lowe Gillian C.,Tan Chee Wee,Giermasz Adam,Tran Huyen,Khoo Teh-Liane,Cockrell Erin,Pepperell Dominic,Chambost Hervé,López Fernández Maria Fernanda,Kazmi Rashid,Majerus Elaine,Skinner Mark W.,Klamroth Robert,Quinn Jennifer,Yu Hua,Wong Wing Yen,Robinson Tara M.,Pipe Steven W.

Funder

BioMarin Pharmaceutical

Publisher

Elsevier BV

Subject

Hematology

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3. A Retrospective Observational Study of Quality of Life in a Northern Greece Population of People with Haemophilia;Life;2024-05-29

4. Gene Therapy in Hemophilia A: Achievements, Challenges, and Perspectives;Seminars in Thrombosis and Hemostasis;2024-04-08

5. Effect of etranacogene dezaparvovec on quality of life for severe and moderately severe haemophilia B participants: Results from the phase III HOPE‐B trial 2 years after gene therapy;Haemophilia;2024-03-10