A review of the rationale for gene therapy for hemophilia A with inhibitors: one-shot tolerance and treatment?-Reference-Cited by-同舟云学术

A review of the rationale for gene therapy for hemophilia A with inhibitors: one-shot tolerance and treatment?

Published:2023-11 Issue:11 Volume:21 Page:3033-3044
ISSN:1538-7836
Container-title:Journal of Thrombosis and Haemostasis
language:en
Short-container-title:Journal of Thrombosis and Haemostasis

Author:

Valentino Leonard A.^ORCID,Ozelo Margareth C.^ORCID,Herzog Roland W.^ORCID,Key Nigel S.^ORCID,Pishko Allyson M.^ORCID,Ragni Margaret V.^ORCID,Samelson-Jones Benjamin J.^ORCID,Lillicrap David^ORCID

Funder

BioMarin Pharmaceutical

Publisher

Elsevier BV

Subject

Hematology

Reference96 articles.

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3. The changing face of immune tolerance induction in haemophilia A with the advent of emicizumab;Carcao;Haemophilia,2019

4. Valoctocogene roxaparvovec gene therapy for hemophilia A;Ozelo;N Engl J Med,2022

5. Disappearance of inhibitor to factor VIII in HIV-infected hemophiliacs with progression to AIDS or severe ARC;Ragni;Transfusion,1989

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3. Immune tolerance induction by hepatic gene transfer: First-in-human evidence;Molecular Therapy;2024-04

4. Haemophilia in the era of novel therapies: Where do inhibitors feature in the new landscape?;Haemophilia;2024-03-27

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