Identification of selective and non-selective C9ORF72 targeting in vivo active siRNAs
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Published:2024-09
Issue:3
Volume:35
Page:102291
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ISSN:2162-2531
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Container-title:Molecular Therapy - Nucleic Acids
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language:en
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Short-container-title:Molecular Therapy - Nucleic Acids
Author:
Gilbert James W.,
Kennedy Zachary,
Godinho Bruno M.D.C.,
Summers Ashley,
Weiss Alexandra,
Echeverria Dimas,
Bramato Brianna,
McHugh Nicholas,
Cooper David,
Yamada Ken,
Hassler Matthew,
Tran Hélène,
Gao Fen Biao,
Brown Robert H.,
Khvorova AnastasiaORCID
Funder
Nihon Kohden America
Anika Therapeutics
NIH