Subretinal gene therapy delays vision loss in a Bardet-Biedl Syndrome type 10 mouse model-Reference-Cited by-同舟云学术

Subretinal gene therapy delays vision loss in a Bardet-Biedl Syndrome type 10 mouse model

Published:2023-03 Issue: Volume:31 Page:164-181
ISSN:2162-2531
Container-title:Molecular Therapy - Nucleic Acids
language:en
Short-container-title:Molecular Therapy - Nucleic Acids

Author:

Hsu Ying^ORCID,Bhattarai Sajag,Thompson Jacob M.,Mahoney Angela,Thomas Jacintha,Mayer Sara K.,Datta Poppy,Garrison Janelle,Searby Charles C.,Vandenberghe Luk H.,Seo Seongjin,Sheffield Val C.,Drack Arlene V.

Publisher

Elsevier BV

Subject

Drug Discovery,Molecular Medicine

Reference45 articles.

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2. BBSome trains remove activated GPCRs from cilia by enabling passage through the transition zone;Ye;J. Cell Biol.,2018

3. Photoreceptor outer segment as a sink for membrane proteins: hypothesis and implications in retinal ciliopathies;Seo;Hum. Mol. Genet.,2017

4. Accumulation of non-outer segment proteins in the outer segment underlies photoreceptor degeneration in Bardet–Biedl syndrome;Datta;Proc. Natl. Acad. Sci. USA,2015

5. BBSome function is required for both the morphogenesis and maintenance of the photoreceptor outer segment;Hsu;PLoS Genet.,2017

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