Editing the core region in HPFH deletions alters fetal and adult globin expression for treatment of β-hemoglobinopathies-Reference-Cited by-同舟云学术

Editing the core region in HPFH deletions alters fetal and adult globin expression for treatment of β-hemoglobinopathies

Published:2023-06 Issue: Volume:32 Page:671-688
ISSN:2162-2531
Container-title:Molecular Therapy - Nucleic Acids
language:en
Short-container-title:Molecular Therapy - Nucleic Acids

Author:

Venkatesan Vigneshwaran,Christopher Abisha Crystal,Rhiel Manuel,Azhagiri Manoj Kumar K.,Babu Prathibha,Walavalkar Kaivalya,Saravanan Bharath,Andrieux Geoffroy,Rangaraj Sumathi,Srinivasan Saranya,Karuppusamy Karthik V.,Jacob Annlin,Bagchi Abhirup,Pai Aswin Anand,Nakamura Yukio,Kurita Ryo,Balasubramanian Poonkuzhali,Pai Rekha,Marepally Srujan Kumar,Mohankumar Kumarasamypet Murugesan,Velayudhan Shaji R.,Boerries Melanie,Notani Dimple,Cathomen Toni,Srivastava Alok,Thangavel Saravanabhavan^ORCID

Publisher

Elsevier BV

Subject

Drug Discovery,Molecular Medicine

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