Curative therapy for hemoglobinopathies: an International Society for Cell & Gene Therapy Stem Cell Engineering Committee review comparing outcomes, accessibility and cost of ex vivo stem cell gene therapy versus allogeneic hematopoietic stem cell transplantation-Reference-Cited by-同舟云学术

Curative therapy for hemoglobinopathies: an International Society for Cell & Gene Therapy Stem Cell Engineering Committee review comparing outcomes, accessibility and cost of ex vivo stem cell gene therapy versus allogeneic hematopoietic stem cell transplantation

Published:2021-12 Issue: Volume: Page:
ISSN:1465-3249
Container-title:Cytotherapy
language:en
Short-container-title:Cytotherapy

Author:

Leonard Alexis^ORCID,Bertaina Alice,Bonfim Carmem,Cohen Sandra,Prockop Susan^ORCID,Purtill Duncan^ORCID,Russell Athena^ORCID,Boelens Jaap Jan^ORCID,Wynn Robert,Ruggeri Annalisa,Abraham Allistair^ORCID

Publisher

Elsevier BV

Subject

Cancer Research,Transplantation,Cell Biology,Genetics(clinical),Oncology,Immunology,Immunology and Allergy

Reference136 articles.

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2. Good engraftment after reduced intensity targeted busulfan‐based conditioning and matched related donor hematopoietic cell transplantation in hemoglobinopathies;Pediatric Blood & Cancer;2024-04-12

3. A systematic review of clinical trials for gene therapies for β-hemoglobinopathy around the world;Cytotherapy;2023-12

4. Outcomes and long-term effects of hematopoietic stem cell transplant in sickle cell disease;Expert Review of Hematology;2023-10-12

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