High-Efficiency, Selection-free Gene Repair in Airway Stem Cells from Cystic Fibrosis Patients Rescues CFTR Function in Differentiated Epithelia-Reference-Cited by-同舟云学术

High-Efficiency, Selection-free Gene Repair in Airway Stem Cells from Cystic Fibrosis Patients Rescues CFTR Function in Differentiated Epithelia

Published:2020-02 Issue:2 Volume:26 Page:161-171.e4
ISSN:1934-5909
Container-title:Cell Stem Cell
language:en
Short-container-title:Cell Stem Cell

Author:

Vaidyanathan Sriram,Salahudeen Ameen A.,Sellers Zachary M.,Bravo Dawn T.,Choi Shannon S.,Batish Arpit,Le Wei,Baik Ron,de la O Sean,Kaushik Milan P.,Galper Noah,Lee Ciaran M.,Teran Christopher A.,Yoo Jessica H.,Bao Gang,Chang Eugene H.,Patel Zara M.,Hwang Peter H.,Wine Jeffrey J.,Milla Carlos E.,Desai Tushar J.,Nayak Jayakar V.,Kuo Calvin J.,Porteus Matthew H.

Funder

California Institute for Regenerative Medicine

Publisher

Elsevier BV

Subject

Cell Biology,Genetics,Molecular Medicine

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