BCL11A +58/+55 enhancer-editing facilitates HSPC engraftment and HbF induction in rhesus macaques conditioned with a CD45 antibody-drug conjugate-Reference-Cited by-同舟云学术

BCL11A +58/+55 enhancer-editing facilitates HSPC engraftment and HbF induction in rhesus macaques conditioned with a CD45 antibody-drug conjugate

Published:2025-02 Issue:2 Volume:32 Page:209-226.e8
ISSN:1934-5909
Container-title:Cell Stem Cell
language:en
Short-container-title:Cell Stem Cell

Author:

Demirci Selami^ORCID,Zeng Jing,Palchaudhuri Rahul,Wu Chuanfeng,Abraham Diana M.,Hayal Taha B.,Essawi Khaled,Nguyen My Anh,Stasula Ulana,Chu Rebecca,Leonard Alexis,Porter Shaina N.,Khan Muhammad Behroz Naeem,Hinojosa Gabriela,Uchida Naoya,Hong Sogun,Lazzarotto Cicera R.,Neri Nola R.,da Silva Lucas Ferreira,Pellin Danilo,Verma Archana,Lanieri Leanne,Bhat Anjali,Hammond Katelyn,Tate Tiffany,Maitland Stacy A.,Sheikhsaran Fatemeh,Bonifacino Aylin C.,Krouse Allen E.,Linde Nathaniel S.,Engels Theresa,Golomb Justin,Tsai Shengdar Q.,Pruett-Miller Shondra M.,Scadden David T.,Dunbar Cynthia E.,Wolfe Scot A.,Donahue Robert E.,Olson Lisa M.,Bauer Daniel E.,Tisdale John F.

Funder

Foundation for the National Institutes of Health

National Heart Lung and Blood Institute

Publisher

Elsevier BV

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