Phase I/II Trial of Liver–derived Mesenchymal Stem Cells in Pediatric Liver–based Metabolic Disorders: A Prospective, Open Label, Multicenter, Partially Randomized, Safety Study of One Cycle of Heterologous Human Adult Liver–derived Progenitor Cells (HepaStem) in Urea Cycle Disorders and Crigler-Najjar Syndrome Patients

Author:

Smets Françoise,Dobbelaere Dries,McKiernan Patrick,Dionisi-Vici Carlo,Broué Pierre,Jacquemin Emmanuel,Lopes Ana Isabel,Gonçalves Isabel,Mandel Hanna,Pawlowska Joanna,Kamińska Diana,Shteyer Eyal,Torre Giuliano,Shapiro Riki,Eyskens François,Clapuyt Philippe,Gissen Paul,Pariente Danièle,Grunewald Stephanie,Yudkoff Marc,Binda Maria Mercedes,Najimi Mustapha,Belmonte Nathalie,de Vos Beatrice,Thonnard Joelle,Sokal Etienne

Publisher

Ovid Technologies (Wolters Kluwer Health)

Subject

Transplantation

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