Biologic and Clinical Efficacy of LentiGlobin for Sickle Cell Disease

Author:

Kanter Julie1,Walters Mark C.1ORCID,Krishnamurti Lakshmanan1,Mapara Markus Y.1,Kwiatkowski Janet L.1,Rifkin-Zenenberg Stacey1,Aygun Banu1,Kasow Kimberly A.1,Pierciey Francis J.1,Bonner Melissa1,Miller Alex1,Zhang Xinyan1,Lynch Jessie1,Kim Dennis1,Ribeil Jean-Antoine1,Asmal Mohammed1,Goyal Sunita1,Thompson Alexis A.1,Tisdale John F.1

Affiliation:

1. From the University of Alabama Birmingham, Birmingham (J.K.); UCSF Benioff Children’s Hospital, Oakland, CA (M.C.W.); Aflac Cancer and Blood Disorders Center, Department of Pediatrics, Children’s Healthcare of Atlanta, Emory University, Atlanta (L.K.); the Division of Hematology–Oncology, Columbia Center for Translational Immunology, Columbia University Medical Center, New York (M.Y.M.), the Division of Pediatric Hematology, Oncology and Cellular Therapy, Cohen Children’s Medical Center, New Hyde Park (B...

Funder

bluebird bio

Publisher

Massachusetts Medical Society

Subject

General Medicine

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