1. Orphan Drugs: the regulatory environment;P Franco;Drug Discovery today,2013
2. Access to cross-border health care services for patients with rare diseases in the European Union;L Aagaard;Orphan Drugs: research and reviews,2014
3. Availability of and access to orphan drugs;A Blankart;Pharmacoeconomics,2011
4. Garau M, Mestre-Ferrandiz J. Access mechanisms for orphan drugs: a comparative study of selected European countries2009. Available from: http://www.raredisease.org.uk/documents/OHEBriefingOrphanDrugs.pdf.
5. Socio-economic burden of rare diseases: A systematic review of cost of illness evidence;A Angelis;Health Policy,2014