Outcomes Following Gene Therapy in Patients With Severe Wiskott-Aldrich Syndrome

Author:

Hacein-Bey Abina Salima1,Gaspar H. Bobby2,Blondeau Johanna3,Caccavelli Laure3,Charrier Sabine4,Buckland Karen2,Picard Capucine5,Six Emmanuelle6,Himoudi Nourredine2,Gilmour Kimberly2,McNicol Anne-Marie2,Hara Havinder2,Xu-Bayford Jinhua7,Rivat Christine2,Touzot Fabien8,Mavilio Fulvio9,Lim Annick10,Treluyer Jean-Marc11,Héritier Sébastien12,Lefrère Francois13,Magalon Jeremy3,Pengue-Koyi Isabelle8,Honnet Géraldine9,Blanche Stéphane12,Sherman Eric A.14,Male Frances14,Berry Charles14,Malani Nirav14,Bushman Frederic D.14,Fischer Alain15,Thrasher Adrian J.2,Galy Anne4,Cavazzana Marina8

Affiliation:

1. Biotherapy Department, Necker Children’s Hospital, Assistance Publique–Hôpitaux de Paris, Paris, France2Biotherapy Clinical Investigation Center, Groupe Hospitalier Universitaire Ouest, Assistance Publique–Hôpitaux de Paris, INSERM, Paris, France3Unité de

2. Section of Molecular and Cellular Immunology, University College London Institute of Child Health, London, England6Department of Clinical Immunology, Hospital National Health Service Foundation Trust, London, England

3. Biotherapy Department, Necker Children’s Hospital, Assistance Publique–Hôpitaux de Paris, Paris, France2Biotherapy Clinical Investigation Center, Groupe Hospitalier Universitaire Ouest, Assistance Publique–Hôpitaux de Paris, INSERM, Paris, France

4. INSERM U951, Unité Mixte de Recherche S951, Molecular Immunology and Innovative Biotherapies, University of Evry, Evry, France8Genethon, Evry, France

5. Centre d’Étude des Déficits Immunitaires, Hôpital Necker-Enfants Malades, Assistance Publique–Hôpitaux de Paris, Paris, France10Paris Descartes–Sorbonne Paris Cité University, Imagine Institute, Paris, France11Immunology and Pediatric Hematology Departmen

6. Paris Descartes–Sorbonne Paris Cité University, Imagine Institute, Paris, France12INSERM Unité Mixte de Recherche 1163, Laboratory of Human Lymphohematopoiesis, Paris, France

7. Department of Clinical Immunology, Hospital National Health Service Foundation Trust, London, England

8. Biotherapy Department, Necker Children’s Hospital, Assistance Publique–Hôpitaux de Paris, Paris, France2Biotherapy Clinical Investigation Center, Groupe Hospitalier Universitaire Ouest, Assistance Publique–Hôpitaux de Paris, INSERM, Paris, France10Paris D

9. Genethon, Evry, France

10. Groupe Immunoscope, Immunology Department, Institut Pasteur, Paris, France

11. Clinical Research Center Necker–Enfants Malades and Cochin Hospital Assistance Publique–Hôpitaux de Paris, Paris Descartes University

12. Paris Descartes–Sorbonne Paris Cité University, Imagine Institute, Paris, France11Immunology and Pediatric Hematology Department, Assistance Publique–Hôpitaux de Paris, Paris, France

13. Biotherapy Department, Necker Children’s Hospital, Assistance Publique–Hôpitaux de Paris, Paris, France

14. Department of Microbiology, University of Pennsylvania School of Medicine, Philadelphia

15. Paris Descartes–Sorbonne Paris Cité University, Imagine Institute, Paris, France11Immunology and Pediatric Hematology Department, Assistance Publique–Hôpitaux de Paris, Paris, France12INSERM Unité Mixte de Recherche 1163, Laboratory of Human Lymphohematop

Publisher

American Medical Association (AMA)

Subject

General Medicine

同舟云学术

1.学者识别学者识别

2.学术分析学术分析

3.人才评估人才评估

"同舟云学术"是以全球学者为主线,采集、加工和组织学术论文而形成的新型学术文献查询和分析系统,可以对全球学者进行文献检索和人才价值评估。用户可以通过关注某些学科领域的顶尖人物而持续追踪该领域的学科进展和研究前沿。经过近期的数据扩容,当前同舟云学术共收录了国内外主流学术期刊6万余种,收集的期刊论文及会议论文总量共计约1.5亿篇,并以每天添加12000余篇中外论文的速度递增。我们也可以为用户提供个性化、定制化的学者数据。欢迎来电咨询!咨询电话:010-8811{复制后删除}0370

www.globalauthorid.com

TOP

Copyright © 2019-2024 北京同舟云网络信息技术有限公司
京公网安备11010802033243号  京ICP备18003416号-3