Assessment of Systemic Delivery of rAAVrh74.MHCK7.micro-dystrophin in Children With Duchenne Muscular Dystrophy-Reference-Cited by-同舟云学术

Assessment of Systemic Delivery of rAAVrh74.MHCK7.micro-dystrophin in Children With Duchenne Muscular Dystrophy

Published:2020-09-01 Issue:9 Volume:77 Page:1122
ISSN:2168-6149
Container-title:JAMA Neurology
language:en
Short-container-title:JAMA Neurol

Author:

Mendell Jerry R.¹²³,Sahenk Zarife¹²³,Lehman Kelly¹²,Nease Carrie¹²,Lowes Linda P.¹²³,Miller Natalie F.¹,Iammarino Megan A.¹,Alfano Lindsay N.¹,Nicholl Amanda¹,Al-Zaidy Samiah²,Lewis Sarah¹⁴,Church Kathleen¹,Shell Richard²,Cripe Linda H.²,Potter Rachael A.¹⁴,Griffin Danielle A.¹⁴,Pozsgai Eric¹⁴,Dugar Ashish⁴,Hogan Mark⁵,Rodino-Klapac Louise R.¹²⁴

Affiliation:

1. Center for Gene Therapy, The Abigail Wexner Research Institute at Nationwide Children’s Hospital, Columbus, Ohio

2. Department of Pediatrics, The Ohio State University, Columbus

3. Department of Neurology, The Ohio State University, Columbus

4. Sarepta Therapeutics Inc, Cambridge, Massachusetts

5. Department of Radiology, Vascular and Interventional Radiology, Nationwide Children's Hospital, Columbus, Ohio

Publisher

American Medical Association (AMA)

Subject

Clinical Neurology

Link

https://jamanetwork.com/journals/jamaneurology/articlepdf/2767086/jamaneurology_mendell_2020_oi_200033_1598965175.46323.pdf