1. Center for Gene Therapy, Nationwide Children’s Hospital, Columbus, Ohio
2. Department of Pediatrics, The Ohio State University, Columbus
3. Department of Neurology, The Ohio State University, Columbus
4. Al-Zaidy and Associates, LLC, Columbus, Ohio
5. Novartis Gene Therapies, Inc, Bannockburn, Illinois
6. Section of Pulmonary Medicine, Department of Pediatrics, Nationwide Children’s Hospital, Columbus, Ohio