Lipid Nanoparticles for Cell-Specific in Vivo Targeted Delivery of Nucleic Acids

Author:

Khalil Ikramy A.12,Younis Mahmoud A.12,Kimura Seigo1,Harashima Hideyoshi1

Affiliation:

1. Faculty of Pharmaceutical Sciences, Hokkaido University

2. Faculty of Pharmacy, Assiut University

Publisher

Pharmaceutical Society of Japan

Subject

Pharmaceutical Science,Pharmacology,General Medicine

Reference130 articles.

1. 1) Vannucci L, Lai M, Chiuppesi F, Ceccherini-Nelli L, Pistello M. Viral vectors: a look back and ahead on gene transfer technology. New Microbiol., 36, 1–22 (2013).

2. 2) Yin H, Kanasty RL, Eltoukhy AA, Vegas AJ, Dorkin JR, Anderson DG. Non-viral vectors for gene-based therapy. Nat. Rev. Genet., 15, 541–555 (2014).

3. 3) Lukashev AN, Zamyatnin AA Jr. Viral vectors for gene therapy: current state and clinical perspectives. Biochemistry (Mosc.), 81, 700–708 (2016).

4. 4) Elsabahy M, Nazarali A, Foldvari M. Non-viral nucleic acid delivery: key challenges and future directions. Curr. Drug Deliv., 8, 235–244 (2011).

5. 5) Rizk M, Tüzmen Ş. Update on the clinical utility of an RNA interference-based treatment: focus on Patisiran. Pharmgenomics Pers. Med., 10, 267–278 (2017).

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