Gene therapy for Duchenne muscular dystrophy: an update on the latest clinical developments
Author:
Affiliation:
1. CHU de Québec research centre, Laval University, Québec, Canada
2. Molecular Medicine Department, Faculty of Medicine, Laval University, Québec, Canada
Funder
Health Research
Publisher
Informa UK Limited
Subject
Pharmacology (medical),Neurology (clinical),General Neuroscience
Link
https://www.tandfonline.com/doi/pdf/10.1080/14737175.2023.2249607
Reference108 articles.
1. The Dystrophin Complex: Structure, Function, and Implications for Therapy
2. The burden, epidemiology, costs and treatment for Duchenne muscular dystrophy: an evidence review
3. Age at onset of first signs or symptoms predicts age at loss of ambulation in Duchenne and Becker Muscular Dystrophy: Data from the MD STARnet
4. Duchenne muscular dystrophy and dystrophin: pathogenesis and opportunities for treatment
5. Dystrophin expression in muscle stem cells regulates their polarity and asymmetric division
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3. Is Cardiac Transplantation Still a Contraindication in Patients with Muscular Dystrophy-Related End-Stage Dilated Cardiomyopathy? A Systematic Review;International Journal of Molecular Sciences;2024-05-13
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