1. Takeda Development Center Americas, Inc, Cambridge, MA, USA
2. Millennium Pharmaceuticals, Inc, a Takeda Company, Cambridge, MA, USA
3. Centre for Outcomes and Experience Research in Children’s Health, Illness and Disability (ORCHID), Great Ormond Street Hospital for Children, London, UK
4. Baxalta GmbH, a Takeda Company, Zürich, Switzerland
5. Hemocentro UNICAMP, University of Campinas, Campinas, SP, Brazil
6. Department of Hemostasis Disorders and Internal Medicine, Institute of Hematology and Transfusion Medicine, Warsaw, Poland